Rita Sattler was awarded a Robert Packard Center for ALS Research Grant: “Role of synaptic dysfunction in C9orf72-mediated pathogenesis in patient-derived iPS neurons and in vivo animal models”
Rita Sattler was awarded a research grant with the Judith & Jean Pape Adams Charitable Foundation: “Preclinical validation of ASO treatment and accompanying biomarker assay for C9orf72 ALS”
Jeffrey Rothstein was awarded a Target ALS New Consortium award in collaboration with Drs. Petrucelli (Mayo Clinic, Florida) and Disney (Scripps Research Institute, Florida): “Discovery of Small Molecules targeting C9ORF72 repeat RNA”