neuron80_2.c1.indd

RNA toxicity from the ALS/FTD C9ORF72 expansion is mitigated by antisense intervention.

J. Donnelly, P.W. Zhang, J.T. Pham, A.R. Haeusler, N.A. Mistry, S. Vidensky, E.L. Daley, E.M. Poth, B.N. Hoover, D.M. Fines, N. Maragakis, P.J. Tienari, L. Petrucelli, B.J. Traynor, J. Wang, F. Rigo, C.F Bennett, S. Blackshaw, R. Sattler, J.D. Rothstein (2013) Neuron 80 (2): 415-428.